2025 / 05

DOI: 10.24075/brsmu.2025.055
Copyright: © 2025 by the authors. Licensee: Pirogov University.
This article is an open access article distributed under the terms and conditions of the Creative Commons Attribution license (CC BY).

OPINION

The terms "dominant" and "recessive" should be avoided due to gene therapy

Gamisonia AM , Rebrikov DV
About authors

Pirogov Russian National Research Medical University (Pirogov University), Moscow, Russia

Correspondence should be addressed: Alina Mukhadinovna Gamisoniya
Ostrovityanova, 1, Moscow, 117997, Russia; ur.liam@ayinosimagma

About paper

Funding: This work was supported by the State Assignment of the Ministry of Health of the Russian Federation, Registration No. 123021500064-0, "Development of technology for personalized gene therapy drugs based on the AAV platform and drugs for the treatment of Sanfilippo syndrome and multiple epiphyseal dysplasia."

Acknowledgements: The authors are grateful to Sergey Glagolev for his critical comments

Author contribution: Gamisoniya AM — analysis and summary of literature data, manuscript writing, manuscript design; Rebrikov DV — critical revision and editing of the manuscript.

Received: 2025-10-23 Accepted: 2025-10-23 Published online: 2025-10-31
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